Terapia genica in emofilia B

Dott.ssa Cristina Santoro
Terapia genica in emofilia B
Steven W Pipe et al. Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B. N Engl J Med. 2023 Feb 23;388(8):706-718. doi: 10.1056/NEJMoa2211644. PMID: 36812434.